Make a tax-deductible donation today.

Without your support, Sasha will never develop - she will be an infant trapped in a woman's body, severely disabled and needing 24/7 care for the rest of her life.

3% Cover the Fee

100% of your donation will fund vital scientific work in the United States, helping to deliver a world-first breakthrough in RNA medicine — the first ever antisense oligonucleotide (ASO) therapy targeting a splicing mutation that causes epilepsy.

SAVING SASHA FROM SLC6A1

SASHA’S CURE WILL HELP MILLIONS

Sasha the Pioneer

Your donation is part of a much bigger picture. Sasha has a splice site mutation (ie, a mutation that affects RNA splicing). 15%+ of all disease-causing mutations are splicing mutations! So when we show that Sasha's mutation can be fixed, that will pave the way to treating millions of people for all kinds of genetic diseases.

This is our only chance to help our daughter. We must fight for her, and millions of other children like her.

BE PART OF A GLOBAL FIRST

IN RNA MEDICINE

The world’s first ASO for

an epilepsy splicing mutation